Center-Authored Papers

Filters: Author is Rawlings, David J  [Clear All Filters]
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Hocum JD, Battrell LR, Maynard R, Adair JE, Beard BC, Rawlings DJ, Kiem H-P, Miller DG, Trobridge GD.  2015.  VISA - Vector Integration Site Analysis server: a web-based server to rapidly identify retroviral integration sites from next-generation sequencing.. BMC bioinformatics. 16:212. Abstract
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Burroughs LM, Nemecek ER, Torgerson TR, Storer BE, Talano J-A, Domm J, Giller RH, Shimamura A, Delaney C, Skoda-Smith S et al..  2014.  Treosulfan-based conditioning and hematopoietic cell transplantation for nonmalignant diseases: a prospective multicenter trial.. Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation. 20(12):1996-2003. Abstract
Tampella G, Kerns HM, Niu D, Singh S, Khim S, Bosch KA, Garrett ME, Moguche A, Evans E, Browning B et al..  2015.  The Tec Kinase-Regulated Phosphoproteome Reveals a Mechanism for the Regulation of Inhibitory Signals in Murine Macrophages.. Journal of immunology (Baltimore, Md. : 1950). Abstract
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Aubert M, Ryu BY, Banks L, Rawlings DJ, Scharenberg AM, Jerome KR.  2011.  Successful targeting and disruption of an integrated reporter lentivirus using the engineered homing endonuclease Y2 I-AniI.. PloS one. 6(2):e16825. Abstract
Burroughs LM, Torgerson TR, Storb R, Carpenter PA, Rawlings DJ, Sanders JE, Scharenberg AM, Skoda-Smith S, Englund J, Ochs HD et al..  2010.  Stable hematopoietic cell engraftment after low-intensity nonmyeloablative conditioning in patients with immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome.. The Journal of allergy and clinical immunology. 126(5):1000-5. Abstract
Singh S, Khan I, Khim S, Seymour B, Sommer K, Wielgosz M, Norgaard Z, Kiem H-P, Adair J, Liggitt D et al..  2017.  Safe and Effective Gene Therapy for Murine Wiskott-Aldrich Syndrome Using an Insulated Lentiviral Vector.. Molecular therapy. Methods & clinical development. 4:1-16. Abstract
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Wang CX, Sather BD, Wang X, Adair J, Khan I, Singh S, Lang S, Adams A, Curinga G, Kiem H-P et al..  2014.  Rapamycin relieves lentiviral vector transduction resistance in human and mouse hematopoietic stem cells.. Blood. 124(6):913-23. Abstract
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Griffith LM, Cowan MJ, Notarangelo LD, Kohn DB, Puck JM, Pai S-Y, Ballard B, Bauer SC, Bleesing JJH, Boyle M et al..  2013.  Primary Immune Deficiency Treatment Consortium (PIDTC) report.. The Journal of allergy and clinical immunology. Abstract
Grier AE, Burleigh S, Sahni J, Clough CA, Cardot V, Choe DC, Krutein MC, Rawlings DJ, Jensen MC, Scharenberg AM et al..  2016.  pEVL: A Linear Plasmid for Generating mRNA IVT Templates With Extended Encoded Poly(A) Sequences.. Molecular therapy. Nucleic acids. 5:e306. Abstract
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Muñoz NM, Beard BC, Ryu BY, Luche RM, Trobridge GD, Rawlings DJ, Scharenberg AM, Kiem H-P.  2012.  Novel reporter systems for facile evaluation of I-SceI-mediated genome editing.. Nucleic acids research. 40(2) Abstract
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Burtner CR, Beard BC, Kennedy DR, Wohlfahrt ME, Adair JE, Trobridge GD, Scharenberg AM, Torgerson TR, Rawlings DJ, Felsburg PJ et al..  2014.  Intravenous injection of a foamy virus vector to correct canine SCID-X1.. Blood. 123(23):3578-84. Abstract
Aubert M, Boyle NM, Stone D, Stensland L, Huang M-L, Magaret AS, Galetto R, Rawlings DJ, Scharenberg AM, Jerome KR.  2014.  In vitro Inactivation of Latent HSV by Targeted Mutagenesis Using an HSV-specific Homing Endonuclease.. Molecular therapy. Nucleic acids. 3:e146. Abstract
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Gwiazda KS, Grier AE, Sahni J, Burleigh SM, Martin U, Yang JG, Popp NA, Krutein MC, Khan IF, Jacoby K et al..  2016.  High efficiency CRISPR/Cas9-mediated gene editing in primary human T-cells using mutant adenoviral E4orf6/E1b55k "helper" proteins.. Molecular therapy : the journal of the American Society of Gene Therapy. Abstract
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Romano Ibarra GS, Paul B, Sather BD, Younan PM, Sommer K, Kowalski JP, Hale M, Stoddard B, Jarjour J, Astrakhan A et al..  2016.  Efficient Modification of the CCR5 Locus in Primary Human T Cells With megaTAL Nuclease Establishes HIV-1 Resistance.. Molecular therapy. Nucleic acids. 5(8):e352. Abstract
Sather BD, Romano Ibarra GS, Sommer K, Curinga G, Hale M, Khan IF, Singh S, Song Y, Gwiazda K, Sahni J et al..  2015.  Efficient modification of CCR5 in primary human hematopoietic cells using a megaTAL nuclease and AAV donor template.. Science translational medicine. 7(307):307ra156. Abstract
Paul B, Ibarra GRS, Hubbard N, Einhaus T, Astrakhan A, Rawlings DJ, Kiem H-P, Peterson CW.  2018.  Efficient Enrichment of Gene-Modified Primary T Cells via CCR5-Targeted Integration of Mutant Dihydrofolate Reductase.. Molecular therapy. Methods & clinical development. 9:347-357. Abstract
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Bandaranayake AD, Correnti C, Ryu BY, Brault M, Strong RK, Rawlings DJ.  2011.  Daedalus: a robust, turnkey platform for rapid production of decigram quantities of active recombinant proteins in human cell lines using novel lentiviral vectors.. Nucleic acids research. 39(21):e143. Abstract
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Certo MT, Gwiazda KS, Kuhar R, Sather B, Curinga G, Mandt T, Brault M, Lambert AR, Baxter SK, Jacoby K et al..  2012.  Coupling endonucleases with DNA end-processing enzymes to drive gene disruption.. Nature methods. 9(10):973-5. Abstract
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Metzler G, Kolhatkar NS, Rawlings DJ.  2015.  BCR and co-receptor crosstalk facilitate the positive selection of self-reactive transitional B cells.. Current opinion in immunology. 37:46-53. Abstract
Kolhatkar NS, Scharping NE, Sullivan JM, Jacobs HM, Schwartz MA, Khim S, Notarangelo LD, Thrasher AJ, Rawlings DJ, Jackson SW.  2015.  B-cell-intrinsic TLR7 signals promote depletion of the marginal zone in a murine model of Wiskott-Aldrich syndrome.. European journal of immunology. Abstract
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Kolhatkar NS, Brahmandam A, Thouvenel CD, Becker-Herman S, Jacobs HM, Schwartz MA, Allenspach EJ, Khim S, Panigrahi AK, Luning Prak ET et al..  2015.  Altered BCR and TLR signals promote enhanced positive selection of autoreactive transitional B cells in Wiskott-Aldrich syndrome.. The Journal of experimental medicine. Abstract