Transplantation outcomes for severe combined immunodeficiency, 2000-2009.

Publication Type:

Journal Article


The New England journal of medicine, Volume 371, Issue 5, p.434-46 (2014)


2014, August 2014, Clinical Research Division


The Primary Immune Deficiency Treatment Consortium was formed to analyze the results of hematopoietic-cell transplantation in children with severe combined immunodeficiency (SCID) and other primary immunodeficiencies. Factors associated with a good transplantation outcome need to be identified in order to design safer and more effective curative therapy, particularly for children with SCID diagnosed at birth.